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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Cardiomyopathy
Homeostasis
Liver
Invivo
Genomic
Myotendinous junction
Animals
Muscle Biology
MiARN
Dystrophie Musculaire de Duchenne DMD
Delivery
CD38
Humans
Long noncoding RNA
Cells
LncARN
Muscle Strength
Dystrophy
Molecular docking
Inhibitors
Clinical trials
Activin Receptors
Muscle development
CTNNB1
Dystrophie musculaire de Becker
DHPR α1S
Calcium Channels
Diseases
Duchenne muscular dystrophy
Immunoglobulin Fc Fragments/pharmacology
Duchenne muscular dystrophy DMD
Energy Metabolism/drug effects
Hear
LncRNA
Ex-vivo
Multi resolution modeling
Exon skipping
Becker BMD muscular dystrophy
Centronuclear myopathy
Dystrophin-EGFP
Muscle
Muscles/physiopathology
Knockout
Cardiomyopathie
Gene Expression Regulation/drug effects
Dystrophie Musculaire de Becker BMD
Morphogenesis
Muscular Dystrophy
Dystrophin central domain
Epigenetics
Multiresolution modeling
Mitochondrial fission
Human Umbilical Vein Endothelial Cells
DMO
Base Sequence
NAD+
Mdx mouse
Génomique
L-Type
Calcium
Male
BMD
Gene modifiers
Cell Line
MES
NNOS
Mice
Allele‐specific silencing therapy
Multi exon skipping
Gene expression
Inbred mdx
Cell homeostasis
Skeletal muscle
CaVβs
Dynamin 2
Animal/physiopathology
Antisense oligonucleotides
Muscular Atrophy
Myogenesis
Dystrophine
Cultured
DMD
Autophagy
CaV subunits
Cell Biology
Muscular dystrophy
LKB1
Becker muscular dystrophy
Metabolism
Long QT
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Molecular Sequence Data
Dystrophin
Inbred C57BL
Hepatocellular carcinoma
Duchenne DMD dystrophy
Becker muscular dystrophy BMD
Modificateurs de gènes
Drp1
Cachexia